Featured Video: Neuromuscular Disease Awareness
Neuromuscular Diseases Awareness: Muscular Dystrophy Assoc. · “Pipeline Of Promise” Treatments: Spinal Muscular Atrophy · Pompe Disease · MDA Let’s Play Gaming (Twitch.tv) · Donate The US Food and Drug Administration (FDA) granted approval of risdiplam (Evrysdi) for the treatment of spinal muscular atrophy (SMA) in pediatric and adult patients. It is the third disease-modifying […]